A Prospective, Non-interventional Study to Evaluate the Efficacy and Safety of Iptacopan in Adults With Paroxysmal Nocturnal Hemoglobinuria (PNH) in Routine Clinical Practice in the Russian Federation
Latest Information Update: 02 Jul 2025
At a glance
- Drugs Iptacopan (Primary)
- Indications Paroxysmal nocturnal haemoglobinuria
- Focus Therapeutic Use
- Acronyms PRIORITY- PNH
- Sponsors Novartis Pharmaceuticals
Most Recent Events
- 02 Jul 2025 New trial record