An Investigator-initiated, Open-label, Dose-escalation Study to Evaluate the Safety, Tolerability, and Preliminary Efficacy of HG005 in Pediatric Patients With Stargardt Disease (STGD1) Caused by Biallelic ABCA4 Mutations
Latest Information Update: 25 Jul 2025
At a glance
- Drugs HG 005 (Primary)
- Indications Stargardt disease
- Focus Adverse reactions
- Acronyms START
- Sponsors HuidaGene Therapeutics
Most Recent Events
- 25 Jul 2025 New trial record