Trial Profile

Expanded Access Protocol for Vatiquinone in Previously Treated Patients With Inherited Mitochondrial Disease

Status: Recruiting

Phase of Trial: Clinical Phase Unknown

Latest Information Update: 16 Sep 2025

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At a glance

Drugs Vatiquinone (Primary)
Indications Leigh disease; Mitochondrial disorders
Focus Adverse reactions; Expanded access
Sponsors PTC Therapeutics

Most Recent Events

16 Sep 2025 New trial record

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