Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT) - PROTECT
Latest Information Update: 03 Oct 2025
At a glance
- Drugs Sirolimus (Primary) ; Carbamazepine; Diazepam; Midazolam; Oxcarbazepine; Phenobarbital; Prednisolone; Propranolol; Propranolol; Sodium valproate; Tetracosactide; Valproic acid; Verapamil; Vigabatrin
- Indications Nervous system heredodegenerative disorders; Tuberous sclerosis
- Focus Therapeutic Use
- Acronyms PROTECT
Most Recent Events
- 03 Oct 2025 New trial record