Trial Profile

A Phase 3 study of votoplam (PTC518)

Status: Planning

Phase of Trial: Phase III

Latest Information Update: 08 Oct 2025

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At a glance

Drugs Votoplam (Primary)
Indications Huntington's disease
Focus Therapeutic Use

Most Recent Events

08 Oct 2025 According to a PTC Therapeutics media release, company continues to collaborate with Novartis on next steps and aims to meet with FDA in Q4 2025 to discuss Phase 3 clinical trial design and potential accelerated approval pathway.
08 Oct 2025 New trial record

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