A Phase 1/2, Open-Label, Multicenter, Dose Finding and Dose Expansion Study to Investigate the Safety, Tolerability, and Efficacy of ALXN2350 Gene Therapy in Adult Participants With BAG3 Mutation Associated Dilated Cardiomyopathy
Latest Information Update: 27 Oct 2025
At a glance
- Drugs ALXN 2350 (Primary)
- Indications Dilated cardiomyopathy
- Focus Adverse reactions
- Acronyms DCMRestore
- Sponsors Alexion AstraZeneca Rare Disease
Most Recent Events
- 27 Oct 2025 New trial record