Managed Access to Investigational Use of AOC 1044 in Participants With DMD Mutations Amenable to Exon 44 Skipping
Latest Information Update: 03 Dec 2025
At a glance
- Drugs Delpacibart zotadirsenor (Primary)
- Indications Duchenne muscular dystrophy
- Focus Expanded access; Therapeutic Use
- Sponsors Avidity Biosciences
Most Recent Events
- 03 Dec 2025 New trial record