Trial Profile

Research Study for Single-Patient Treatment of Cree Leukoencephalopathy/Vanishing White Matter Disease

Status: Active, no longer recruiting

Phase of Trial: Phase 0

Latest Information Update: 15 Dec 2025

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At a glance

Drugs Fosigotifator (Primary)
Indications Leukoencephalopathies
Focus Expanded access; Therapeutic Use

Most Recent Events

15 Dec 2025 New trial record

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