An Open-Label Study of Donidalorsen in Pediatric Patients Age 2 to Less Than 12 Years Old With Hereditary Angioedema
Latest Information Update: 29 Dec 2025
At a glance
- Drugs Donidalorsen (Primary)
- Indications Hereditary angioedema
- Focus Adverse reactions; Pharmacokinetics; Registrational
- Sponsors Ionis Pharmaceuticals
Most Recent Events
- 29 Dec 2025 New trial record