A Clinical Exploration Study of Adeno-Associated Virus Vector Expressing Human Phenylalanine Hydroxylase Gene in Adult Classical Phenylketonuria
Latest Information Update: 15 Jan 2026
At a glance
- Drugs GS 1168 (Primary)
- Indications Phenylketonuria
- Focus Adverse reactions
- Sponsors Gritgen Therapeutics
Most Recent Events
- 15 Jan 2026 New trial record