A Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome, Comprising a Randomized, Double-Blind, Placebo-Controlled, Parallel-Group Period Followed by an Open-Label Treatment Period
Latest Information Update: 22 Jan 2026
At a glance
- Drugs Trofinetide (Primary)
- Indications Rett syndrome
- Focus Therapeutic Use
- Sponsors Acadia Pharmaceuticals
Most Recent Events
- 22 Jan 2026 New trial record