A Phase 1, Multicenter, Open-Label Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
Latest Information Update: 28 Jan 2026
At a glance
- Drugs DNL 952 (Primary)
- Indications Glycogen storage disease type II
- Focus Adverse reactions
- Sponsors Denali Therapeutics Inc
Most Recent Events
- 28 Jan 2026 New trial record