A Prospective, Single-center, Open-label, Single-arm Clinical Study to Evaluate the Safety and Efficacy of CS-121, an In Vivo Base Editing Therapy Delivered by Lipid Nanoparticles Targeting APOC3, in Children and Adolescents With Hyperchylomicronemia
Latest Information Update: 05 Feb 2026
At a glance
- Drugs CS 121 (Primary)
- Indications Hyperlipoproteinaemia type I
- Focus Adverse reactions
Most Recent Events
- 05 Feb 2026 New trial record