Trial Profile

A phase 3 study of Batten-1 in Juvenile Batten disease.

Status: Planning

Phase of Trial: Phase III

Latest Information Update: 19 Feb 2026

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At a glance

Drugs BBDF 101 (Primary)
Indications Neuronal ceroid lipofuscinosis
Focus Therapeutic Use

Most Recent Events

19 Feb 2026 New trial record
11 Feb 2026 According to the Biocodex, Theranexus media release, Batten-1 is currently in preparation for phase 3 (start planned in 2026). Juvenile Batten disease

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