A Phase IIb, Monocentric, Non-Profit, Open-label Trial for the Intrathecal Administration of AAV9/AP4M1 for Hereditary Spastic Paraplegia Type 50 (SPG50) - AAV9/AP4M1-ITA-01
Latest Information Update: 19 Feb 2026
At a glance
- Drugs Melpida-Elpida Therapeutics (Primary)
- Indications Hereditary-spastic paraplegia; Paraplegia
- Focus Therapeutic Use
- Acronyms AAV9/AP4M1-ITA-01
Most Recent Events
- 19 Feb 2026 New trial record