An Observational Study to Assess Long-Term Safety of Danicopan Add-on Therapy in Patients With Paroxysmal Nocturnal Hemoglobinuria: Analysis of IPIG-Registry Data
Latest Information Update: 23 Feb 2026
At a glance
- Drugs Danicopan (Primary) ; Eculizumab; Ravulizumab
- Indications Paroxysmal nocturnal haemoglobinuria
- Focus Adverse reactions
- Sponsors Alexion AstraZeneca Rare Disease
Most Recent Events
- 23 Feb 2026 New trial record