A Study to Assess Long-Term Safety of Danicopan Add-on Therapy in Participants With Paroxysmal Nocturnal Hemoglobinuria: Analysis of International PNH Interest Group (IPIG)-Registry Data
Latest Information Update: 24 Feb 2026
At a glance
- Drugs Danicopan (Primary) ; Eculizumab (Primary) ; Ravulizumab (Primary)
- Indications Paroxysmal nocturnal haemoglobinuria
- Focus Adverse reactions
- Sponsors Alexion AstraZeneca Rare Disease
Most Recent Events
- 24 Feb 2026 New trial record