Trial Profile

A clinical study of ATX-04 for treatment of Pompe Disease

Status: Completed

Phase of Trial: Phase I

Latest Information Update: 10 Mar 2026

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At a glance

Drugs Clenbuterol (Primary)
Indications Glycogen storage disease type II
Focus Proof of concept; Therapeutic Use

Most Recent Events

10 Mar 2026 New trial record
23 Feb 2026 According to an Avenue Therapeutics media release, this study was conducted at duke university and led by Principal Investigator Dwight D. Koeberl.

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