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An Open-Label Extension Study to Evaluate the Long-term Safety and Efficacy of Weekly Intravenous Infusions of BMN 351 in Participants with Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping

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Trial Profile

An Open-Label Extension Study to Evaluate the Long-term Safety and Efficacy of Weekly Intravenous Infusions of BMN 351 in Participants with Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping

Status: Recruiting
Phase of Trial: Phase II

Latest Information Update: 19 May 2026

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At a glance

  • Drugs BMN 351 (Primary)
  • Indications Duchenne muscular dystrophy
  • Focus Adverse reactions
  • Sponsors BioMarin Pharmaceutical

Most Recent Events

  • 19 May 2026 Planned number of patients changed from 13 to 18.
  • 14 May 2026 Status changed from not yet recruiting to recruiting.
  • 03 Apr 2026 New trial record

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