An Open-Label Extension Study to Evaluate the Long-term Safety and Efficacy of Weekly Intravenous Infusions of BMN 351 in Participants with Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping
Latest Information Update: 03 Apr 2026
At a glance
- Drugs BMN 351 (Primary)
- Indications Duchenne muscular dystrophy
- Focus Adverse reactions
- Sponsors BioMarin Pharmaceutical
Most Recent Events
- 03 Apr 2026 New trial record