A Phase 3, Double-Blind, Randomized, Placebo-Controlled, Multicenter Study Evaluating the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Subjects With α- or β-Non-Transfusion-Dependent Thalassemia
Latest Information Update: 13 Apr 2026
At a glance
- Drugs Mitapivat (Primary)
- Indications Alpha-thalassaemia; Beta-thalassaemia
- Focus Therapeutic Use
- Acronyms ENERGIZEKids
- Sponsors Agios Pharmaceuticals
Most Recent Events
- 13 Apr 2026 New trial record