Trial Profile

A Phase 3, Double-Blind, Randomized, Placebo-Controlled, Multicenter Study Evaluating the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Subjects With α- or β-Non-Transfusion-Dependent Thalassemia

Status: Not yet recruiting

Phase of Trial: Phase III

Latest Information Update: 29 May 2026

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At a glance

12 May 2026 According to an Agios Pharmaceuticals media release, data from this trial will be presented at the 31st European Hematology Association (EHA) Congress (EHA 2026) in Stockholm, Sweden, June 11-14, 2026.
13 Apr 2026 New trial record

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