Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH

Trial Profile

Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH

Recruiting
Phase of Trial: Phase I/II

Latest Information Update: 04 Aug 2017

At a glance

  • Drugs ABO 102 (Primary)
  • Indications Mucopolysaccharidosis III
  • Focus Adverse reactions; First in man
  • Sponsors Abeona therapeutics
  • Most Recent Events

    • 19 May 2017 Results from this trial published in an Abeona Therapeutics Media Release.
    • 19 May 2017 According to an Abeona Therapeutics media release, top-line data from this trial will be presented at upcoming conference of American Society Gene and Cell Therapy (ASGCT).
    • 12 May 2017 Updated data (n=3 Cohort 1, n=2 Cohort 2) from this trial published in an Abeona Therapeutics Media Release.
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