Research Programme: Adeno Associated Virus capsids - Apertura Gene Therapy
Alternative Names: AAV capsids - Apertura Gene Therapy; Adeno-Associated Virus capsids - Apertura Gene TherapyLatest Information Update: 13 Feb 2024
At a glance
- Originator Apertura Gene Therapy
- Class Gene therapies
- Mechanism of Action CD71 antigen modulators; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research CNS disorders