The Paroxysmal Nocturnal Hemoglobinuria Early Access Treatment Protocol
Latest Information Update: 03 Nov 2023
At a glance
- Drugs Eculizumab (Primary)
- Indications Paroxysmal nocturnal haemoglobinuria
- Focus Expanded access; Therapeutic Use
- Acronyms EMBRACE
- Sponsors Alexion Pharmaceuticals
Most Recent Events
- 19 Jun 2017 New trial record