A Phase I/II Multicenter, Open-Label Study to Evaluate the Safety, Tolerability, and Pharmacodynamics of RGX-121 in Children 5 Years of Age and Older With MPS II (Hunter Syndrome)
Latest Information Update: 31 Jan 2025
At a glance
- Drugs Clemidsogene lanparvovec (Primary) ; Clemidsogene lanparvovec (Primary)
- Indications Mucopolysaccharidosis II
- Focus Adverse reactions
- Sponsors REGENXBIO
Most Recent Events
- 28 Jan 2025 Status changed from active, no longer recruiting to completed.
- 17 Nov 2023 Planned End Date changed from 1 Jan 2024 to 1 Nov 2025.
- 17 Nov 2023 Planned primary completion date changed from 1 May 2023 to 1 May 2024.